| 1 | VRDNViridian Therapeutics, Inc.\DE | 100 | 23360% | -484% | $2.1B | — |
| 2 | IDYAIDEAYA Biosciences, Inc. | 98 | 3024% | -62% | $3.6B | — |
| 3 | LQDALiquidia Corp | 95 | 1031% | 8% | $7.0B | — |
| 4 | TGTXTG THERAPEUTICS, INC. | 93 | 87% | 66% | $8.2B | 5 |
| 5 | ARQTArcutis Biotherapeutics, Inc. | 91 | 123% | -1% | $3.2B | 4 |
| 6 | TVTXTravere Therapeutics, Inc. | 88 | 110% | -4% | $5.3B | 7 |
| 7 | PTCTPTC THERAPEUTICS, INC. | 86 | 115% | -23% | $6.9B | — |
| 8 | LGNDLIGAND PHARMACEUTICALS INC | 84 | 60% | 46% | $6.4B | — |
| 9 | AUPHAurinia Pharmaceuticals Inc. | 81 | 20% | 100% | $2.0B | 7 |
| 10 | KNSAKiniksa Pharmaceuticals International, plc | 79 | 60% | 10% | $5.0B | 7 |
| 11 | TLXTelix Pharmaceuticals Ltd | 77 | 56% | -1% | $4.0B | — |
| 12 | STOKStoke Therapeutics, Inc. | 74 | 405% | -529% | $2.0B | — |
| 13 | LEGNLegend Biotech Corp | 72 | 64% | -29% | $5.8B | — |
| 14 | CPRXCATALYST PHARMACEUTICALS, INC. | 70 | 20% | 37% | $3.9B | 5 |
| 15 | ABCLAbCellera Biologics Inc. | 67 | 161% | -182% | $2.5B | — |
| 16 | ACADACADIA PHARMACEUTICALS INC | 65 | 12% | 34% | $4.4B | 6 |
| 17 | HRMYHarmony Biosciences Holdings, Inc. | 63 | 22% | 16% | $2.2B | 5 |
| 18 | CORTCORCEPT THERAPEUTICS INC | 60 | 13% | 14% | $9.7B | 4 |
| 19 | INDVIndivior Pharmaceuticals, Inc. | 58 | 4% | 17% | $4.7B | 5 |
| 20 | AMRXAmneal Pharmaceuticals, Inc. | 56 | 8% | 6% | $5.5B | 8 |
| 21 | GRFSGrifols SA | 53 | 9% | 3% | $4.9B | — |
| 22 | PBHPrestige Consumer Healthcare Inc. | 51 | -4% | 17% | $2.3B | 5 |
| 23 | SUPNSUPERNUS PHARMACEUTICALS, INC. | 49 | 9% | -4% | $2.8B | 4 |
| 24 | RGCRegencell Bioscience Holdings Ltd | 47 | -1% | 4% | $3.1B | — |
| 25 | ALKSAlkermes plc. | 44 | -5% | 10% | $9.1B | 7 |