| 1 | VRDNViridian Therapeutics, Inc.DE | 100 | 23360% | -484% | $2.1B | — |
| 2 | IDYAIDEAYA Biosciences, Inc. | 99 | 3024% | -62% | $3.6B | — |
| 3 | LQDALiquidia Corp | 98 | 1031% | 8% | $7.0B | — |
| 4 | IBRXImmunityBio, Inc. | 98 | 668% | -310% | $9.9B | 5 |
| 5 | TARSTarsus Pharmaceuticals, Inc. | 97 | 147% | -15% | $2.8B | — |
| 6 | TGTXTG THERAPEUTICS, INC. | 96 | 87% | 66% | $8.2B | 5 |
| 7 | ARQTArcutis Biotherapeutics, Inc. | 95 | 123% | -1% | $3.2B | 4 |
| 8 | TVTXTravere Therapeutics, Inc. | 94 | 110% | -4% | $5.3B | 7 |
| 9 | BLLNBillionToOne, Inc. | 93 | 100% | 8% | $5.5B | 7 |
| 10 | CAICaris Life Sciences, Inc. | 92 | 97% | 4% | $5.2B | — |
| 11 | PTCTPTC THERAPEUTICS, INC. | 92 | 115% | -23% | $6.9B | — |
| 12 | BEAMBeam Therapeutics Inc. | 91 | 120% | -40% | $3.6B | — |
| 13 | LGNDLIGAND PHARMACEUTICALS INC | 90 | 60% | 46% | $6.4B | — |
| 14 | AUPHAurinia Pharmaceuticals Inc. | 89 | 20% | 100% | $2.0B | 7 |
| 15 | CHECHEMED CORP | 88 | 65% | 10% | $6.5B | 6 |
| 16 | KNSAKiniksa Pharmaceuticals International, plc | 88 | 60% | 10% | $5.0B | 7 |
| 17 | HIMSHims & Hers Health, Inc. | 87 | 59% | 5% | $8.5B | 4 |
| 18 | BCRXBIOCRYST PHARMACEUTICALS INC | 86 | 94% | -52% | $2.5B | 7 |
| 19 | TMDXTransMedics Group, Inc. | 85 | 37% | 27% | $2.4B | 7 |
| 20 | TLXTelix Pharmaceuticals Ltd | 84 | 56% | -1% | $4.0B | — |
| 21 | HALOHALOZYME THERAPEUTICS, INC. | 83 | 38% | 23% | $9.4B | 5 |
| 22 | STOKStoke Therapeutics, Inc. | 82 | 405% | -529% | $2.0B | — |
| 23 | ALHCAlignment Healthcare, Inc. | 82 | 46% | -0% | $4.9B | — |
| 24 | LEGNLegend Biotech Corp | 81 | 64% | -29% | $5.8B | — |
| 25 | CPRXCATALYST PHARMACEUTICALS, INC. | 80 | 20% | 37% | $3.9B | 5 |