| 1 | VRDNViridian Therapeutics, Inc.DE | 100 | 23360% | -484% | $2.1B | — |
| 2 | IDYAIDEAYA Biosciences, Inc. | 99 | 3024% | -62% | $3.6B | — |
| 3 | LQDALiquidia Corp | 98 | 1031% | 8% | $7.0B | — |
| 4 | IBRXImmunityBio, Inc. | 97 | 668% | -310% | $9.9B | 5 |
| 5 | TARSTarsus Pharmaceuticals, Inc. | 96 | 147% | -15% | $2.8B | — |
| 6 | TGTXTG THERAPEUTICS, INC. | 95 | 87% | 66% | $8.2B | 5 |
| 7 | ARQTArcutis Biotherapeutics, Inc. | 93 | 123% | -1% | $3.2B | 4 |
| 8 | TVTXTravere Therapeutics, Inc. | 92 | 110% | -4% | $5.3B | 7 |
| 9 | PTCTPTC THERAPEUTICS, INC. | 91 | 115% | -23% | $6.9B | — |
| 10 | BEAMBeam Therapeutics Inc. | 90 | 120% | -40% | $3.6B | — |
| 11 | LGNDLIGAND PHARMACEUTICALS INC | 89 | 60% | 46% | $6.4B | — |
| 12 | AUPHAurinia Pharmaceuticals Inc. | 88 | 20% | 100% | $2.0B | 7 |
| 13 | KNSAKiniksa Pharmaceuticals International, plc | 87 | 60% | 10% | $5.0B | 7 |
| 14 | BCRXBIOCRYST PHARMACEUTICALS INC | 86 | 94% | -52% | $2.5B | 7 |
| 15 | TLXTelix Pharmaceuticals Ltd | 85 | 56% | -1% | $4.0B | — |
| 16 | HALOHALOZYME THERAPEUTICS, INC. | 84 | 38% | 23% | $9.4B | 5 |
| 17 | STOKStoke Therapeutics, Inc. | 83 | 405% | -529% | $2.0B | — |
| 18 | LEGNLegend Biotech Corp | 82 | 64% | -29% | $5.8B | — |
| 19 | CPRXCATALYST PHARMACEUTICALS, INC. | 80 | 20% | 37% | $3.9B | 5 |
| 20 | ADPTAdaptive Biotechnologies Corp | 79 | 55% | -17% | $3.4B | 6 |
| 21 | GLUEMonte Rosa Therapeutics, Inc. | 78 | 64% | -31% | $2.0B | — |
| 22 | ADMAADMA BIOLOGICS, INC. | 77 | 20% | 32% | $2.1B | 5 |
| 23 | ABCLAbCellera Biologics Inc. | 76 | 161% | -182% | $2.5B | — |
| 24 | ACADACADIA PHARMACEUTICALS INC | 75 | 12% | 34% | $4.4B | 6 |
| 25 | HRMYHarmony Biosciences Holdings, Inc. | 74 | 22% | 16% | $2.2B | 5 |